Recently Approved Cell-Based Gene Therapies Demonstrate Innovation in Sickle Cell Disease Treatment
This white paper offers a comprehensive primer on the burden of SCD, the patient journey, and current and emerging treatment options.
Resource Guide for Patients Living with Rare Diseases
Access this essential Rare Disease Patient Resource Guide to get comprehensive information on advocacy groups, community connections, clinical trial options, and navigating your diagnosis.
Integrated REMS and Patient Support Services Solution for Complex Rare Disease
Discover how UBC has been the single point of contact for over 10 years to reduce program risk and burden through multiservice governance for 28,000 patients.
First-in-Class Therapy Succeeds with Personalized Patient Services
Learn how an integrated reimbursement and clinical support hub for a first-in-class Sickle Cell Disease therapy achieved 15% higher adherence and overcame patient trust barriers.
Unlock the Full Potential of Evidence Generation in Rare Disease Studies
Learn how real-world data and real-world evidence can transform rare disease study design. Discover patient-centric strategies for recruitment, decentralized elements, and accelerating regulatory success.
