Recently Approved Cell-Based Gene Therapies Demonstrate Innovation in Sickle Cell Disease Treatment
This white paper offers a comprehensive primer on the burden of SCD, the patient journey, and current and emerging treatment options.
Planning Real-World Studies to Support Cell and Gene Therapy Evidence Generation Needs
As the cell and gene therapy pipeline evolves, manufacturers are now faced with the need to provide long-term safety and efficacy data.
Navigating the Complexity of Gene Therapy
Learn how UBC reduced patient access hurdles with a tailored case management approach for a lifesaving SMA treatment.
